Accelerating access to gene therapy
for ultra-rare genetic disorders.
Since the discovery and development of new, innovative genetic medicines focus mainly on larger patient populations, we strive to provide children with ultra-rare genetic conditions with the same level of access. CCF brings a network of scientific experts, technology resources, and affordable manufacturing capacity to expand options with three core areas of focus:
- Providing financial support to accelerate the advancement of gene therapy clinical trials for ultra-rare genetic diseases.
- Supporting the open-source data model and standard protocols across the broader gene therapy community.
- Removing the burden for children and families to access to life-altering clinical trials around the world.
CCF is building a bridge for children with ultra-rare disorders to ensure no child is left behind. The US-based Columbus Children’s Foundation was started in 2018 and operates in Chapel Hill, NC with collaborations throughout the U.S. and abroad.
Meet the Ultra Rare Celebrity Jam Board of Directors

Staff Member 1
Job Title
Company name

Staff Member 2
Job Title
Company name

Staff Member 2
Job Title
Company name

Board Member 2
Job Title
Company name

Board Member 2
Job Title
Company name

Board Member 2
Job Title
Company name